Gene Therapy for Leber's Hereditary Optic Neuropathy: Time to Include a True Placebo Arm?

Qiancheng Wang, Dan Milea, Andrew G. Lee

Research output: Contribution to journalEditorialpeer-review

1 Scopus citations
Original languageEnglish (US)
Pages (from-to)A11-A12
JournalAmerican Journal of Ophthalmology
Volume241
DOIs
StatePublished - Sep 2022

Keywords

  • Genetic Therapy
  • Humans
  • Mutation
  • Optic Atrophy, Hereditary, Leber/genetics
  • Placebos
  • Visual Acuity

ASJC Scopus subject areas

  • Ophthalmology

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